Functional correction and reversal of MPS IIIA in a mouse model by an intravenous hSGSH gene delivery using a self-complementary AAV9 vector

✍ Scribed by McCarty, Douglas M.; Zaraspe, Kimberly; Murrey, Darren; Ware, Tierra; Fu, Haiyan

• Book ID: 122278564
• Publisher: Elsevier Science
• Year: 2014
• Tongue: English
• Weight: 52 KB
• Volume: 111
• Category: Article
• ISSN: 1096-7192
• DOI: 10.1016/j.ymgme.2013.12.173