## Abstract ## Background Viruses are being exploited as vectors to deliver therapeutic genetic information into target cells. The success of this approach will depend on the ability to overcome current limitations, especially in terms of safety and efficiency, through molecular engineering of the
Feasibility of gene therapy in Gaucher disease using an adeno-associated virus vector
✍ Scribed by Young Bin Hong; Eun Young Kim; Han-Wook Yoo; Sung-Chul Jung
- Publisher
- Nature Publishing Group
- Year
- 2004
- Tongue
- English
- Weight
- 266 KB
- Volume
- 49
- Category
- Article
- ISSN
- 1435-232X
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