Evidence of Multiyear Factor IX Expression by AAV-Mediated Gene Transfer to Skeletal Muscle in an Individual with Severe Hemophilia B

✍ Scribed by JIANG, H; PIERCE, G; OZELO, M; DEPAULA, E; VARGAS, J; SMITH, P; SOMMER, J; LUK, A; MANNO, C; HIGH, K

• Book ID: 127249647
• Publisher: Nature Publishing Group
• Year: 2006
• Tongue: English
• Weight: 242 KB
• Volume: 14
• Category: Article
• ISSN: 1525-0016
• DOI: 10.1016/j.ymthe.2006.05.004