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Enzyme replacement therapy in two patients with an advanced severe (Hurler) phenotype of mucopolysaccharidosis I

✍ Scribed by Visnja Tokic; Ingeborg Barisic; Nevenka Huzjak; Giorgie Petkovic; Ksenija Fumic; Eduard Paschke

Publisher: Springer
Year: 2006
Tongue: English
Weight: 138 KB
Volume: 166
Category: Article
ISSN: 0340-6997
DOI: 10.1007/s00431-006-0316-8

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