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Enzyme replacement therapy attenuates disease progression in two Japanese siblings with mucopolysaccharidosis type VI

✍ Scribed by Mahoko Furujo; Toshihide Kubo; Motomichi Kosuga; Torayuki Okuyama

Book ID: 116989433
Publisher: Elsevier Science
Year: 2011
Tongue: English
Weight: 974 KB
Volume: 104
Category: Article
ISSN: 1096-7192
DOI: 10.1016/j.ymgme.2011.08.029

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