## Abstract ## Background Directing splicing using oligonucleotides constitutes a promising therapeutic tool for a variety of diseases such as β‐thalassemia, cystic fibrosis, and certain cancers. The rationale is to block aberrant splice sites, thus directing the splicing of the pre‐mRNA towards t
Enhanced delivery of cell-penetrating peptide–peptide nucleic acid conjugates by endosomal disruption
✍ Scribed by Shiraishi, Takehiko; Nielsen, Peter E
- Book ID
- 109946105
- Publisher
- Nature Publishing Group
- Year
- 2006
- Tongue
- English
- Weight
- 141 KB
- Volume
- 1
- Category
- Article
- ISSN
- 1750-2799
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