Early Treatment With Alglucosidase Alfa Prolongs Long-Term Survival of Infants With Pompe Disease

✍ Scribed by Kishnani, Priya S; Corzo, Deya; Leslie, Nancy D; Gruskin, Daniel; van der Ploeg, Ans; Clancy, John P; Parini, Rosella; Morin, Gilles; Beck, Michael; Bauer, Mislen S; Jokic, Mikael; Tsai, Chen-En; Tsai, Brian W H; Morgan, Claire; O'Meara, Tara; Richards, Susan; Tsao, Elisa C; Mandel, Hanna

• Book ID: 121682575
• Publisher: Nature Publishing Group
• Year: 2009
• Tongue: English
• Weight: 483 KB
• Volume: 66
• Category: Article
• ISSN: 0031-3998
• DOI: 10.1203/pdr.0b013e3181b24e94