✦ LIBER ✦

Correction of junctional epidermolysis bullosa by transplantation of genetically modified epidermal stem cells

✍ Scribed by Mavilio, Fulvio; Pellegrini, Graziella; Ferrari, Stefano; Di Nunzio, Francesca; Di Iorio, Enzo; Recchia, Alessandra; Maruggi, Giulietta; Ferrari, Giuliana; Provasi, Elena; Bonini, Chiara

Book ID: 109932935
Publisher: Nature Publishing Group
Year: 2006
Tongue: English
Weight: 506 KB
Volume: 12
Category: Article
ISSN: 1078-8956
DOI: 10.1038/nm1504

No coin nor oath required. For personal study only.

📜 SIMILAR VOLUMES

Correction of anemia in uremic mice by g

Correction of anemia in uremic mice by genetically modified peritoneal mesothelial cells

✍ Einbinder, Tom; Sufaro, Yuval; Yusim, Igor; Byk, Gerardo; Passlick-Deetjen, Jutt 📂 Article 📅 2003 🏛 Nature Publishing Group 🌐 English ⚖ 324 KB

## Background: During peritoneal dialysis, mesothelial cells become detached from the peritoneum and accumulate in the dialysate. our aim was to evaluate the potential of peritoneal effluent (pf)-derived human peritoneal mesothelial cells (hpmc) as target for gene therapy. we used erythropoietin (e

Functional aspects of factor VIII expres

Functional aspects of factor VIII expression after transplantation of genetically-modified hematopoietic stem cells for hemophilia A

✍ Lucienne M. Ide; Neal N. Iwakoshi; Bagirath Gangadharan; Shawn Jobe; Robert Moot 📂 Article 📅 2010 🏛 John Wiley and Sons 🌐 English ⚖ 475 KB

## Abstract ## Background Major complications with respect to the development of gene therapy treatments for hemophilia A include low factor VIII (fVIII) expression and humoral immune responses resulting in inhibitory anti‐fVIII antibodies. We previously achieved sustained curative fVIII activity

Expression of CD95 on mature leukocytes

Expression of CD95 on mature leukocytes of MRL/lpr mice after transplantation of genetically modified bone marrow stem cells

✍ Elena Federzoni; Grace Gordon; Stefan Müller; Inès Schmid; Hans-Uwe Simon; Shida 📂 Article 📅 2008 🏛 Elsevier Science 🌐 English ⚖ 335 KB

Chromosomal analysis of inactivation of

Chromosomal analysis of inactivation of stem cells by transplantation of mixed bone marrow from genetically different donors

✍ R. M. Khaitov 📂 Article 📅 1970 🏛 Springer US 🌐 English ⚖ 199 KB

Superparamagnetic iron oxide labeling of

Superparamagnetic iron oxide labeling of spinal cord neural stem cells genetically modified by nerve growth factor-β

✍ Deqiang Lei; Hongyang Zhao; Xingli Deng; Ruen Liu; Fangcheng Zhang; Dongxiao Yao 📂 Article 📅 2009 🏛 Springer-Verlag 🌐 Chinese ⚖ 487 KB

Brain transplantation of genetically eng

Brain transplantation of genetically engineered human neural stem cells globally corrects brain lesions in the mucopolysaccharidosis type VII mouse

✍ Xing-Li Meng; Jin-Song Shen; Toya Ohashi; Hiroshi Maeda; Seung Up Kim; Yoshikats 📂 Article 📅 2003 🏛 John Wiley and Sons 🌐 English ⚖ 547 KB

## Abstract In the present study, we investigated the feasibility of using human neural stem cells (NSCs) in the treatment of diffuse central nervous system (CNS) alterations in a murine model of mucopolysaccharidosis VII (MPS VII), a lysosomal storage disease caused by a genetic defect in the β‐gl