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Clinical effect of sebelipase alfa on survival and growth in infants with lysosomal acid lipase deficiency (Wolman disease)

✍ Scribed by Valayannopoulos, Vassili; Plantaz, Dominique; Vara, Roshni; Eckert, Stephen; Tripuraneni, Radhika; Schneider, Eugene; Quinn, Anthony G.; Le Quan Sang, Kim-Hanh; Brassier, Anaïs; Arnoux, Jean-Baptiste; White, Fiona; Breen, Catherine; Jones, Simon A.

Book ID: 122174614
Publisher: Elsevier Science
Year: 2014
Tongue: English
Weight: 45 KB
Volume: 111
Category: Article
ISSN: 1096-7192
DOI: 10.1016/j.ymgme.2013.12.268

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