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Chemical chaperone therapy: clinical effect in murine GM1-gangliosidosis

✍ Scribed by Yoshiyuki Suzuki; Satoshi Ichinomiya; Mieko Kurosawa; Masato Ohkubo; Hiroshi Watanabe; Hiroyuki Iwasaki; Junichiro Matsuda; Yoko Noguchi; Kazuhiro Takimoto; Masayuki Itoh; Miho Tabe; Masami Iida; Takatoshi Kubo; Seiichiro Ogawa; Eiji Nanba; Katsumi Higaki; Kousaku Ohno; Roscoe O. Brady

Publisher: John Wiley and Sons
Year: 2007
Tongue: English
Weight: 166 KB
Volume: 62
Category: Article
ISSN: 0364-5134
DOI: 10.1002/ana.21284

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