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Characterization of differential tissue GAA content and CI-M6PR/IGF2R expression using autopsy material obtained from 2 patients with CRIM-negative infantile Pompe disease treated with ERT

✍ Scribed by Prater, Sean; Banugaria, Suhrad; Dai, Jian; Bali, Deeksha; Proia, Alan; Kishnani, Priya


Book ID
121933795
Publisher
Elsevier Science
Year
2013
Tongue
English
Weight
96 KB
Volume
108
Category
Article
ISSN
1096-7192

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