Bifunctional RNAs Targeting the Intronic Splicing Silencer N1 Increase SMN Levels and Reduce Disease Severity in an Animal Model of Spinal Muscular Atrophy

✍ Scribed by Osman, Erkan Y; Yen, Pei-Fen; Lorson, Christian L

• Book ID: 127342575
• Publisher: Nature Publishing Group
• Year: 2012
• Tongue: English
• Weight: 313 KB
• Volume: 20
• Category: Article
• ISSN: 1525-0016
• DOI: 10.1038/mt.2011.232