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Ataluren for the treatment of nonsense-mutation cystic fibrosis: a randomised, double-blind, placebo-controlled phase 3 trial

✍ Scribed by Kerem, Eitan; Konstan, Michael W; De Boeck, Kris; Accurso, Frank J; Sermet-Gaudelus, Isabelle; Wilschanski, Michael; Elborn, J Stuart; Melotti, Paola; Bronsveld, Inez; Fajac, Isabelle; Malfroot, Anne; Rosenbluth, Daniel B; Walker, Patricia A; McColley, Susanna A; Knoop, Christiane; Quattrucci, Serena; Rietschel, Ernst; Zeitlin, Pamela L; Barth, Jay; Elfring, Gary L; Welch, Ellen M; Branstrom, Arthur; Spiegel, Robert J; Peltz, Stuart W; Ajayi, Temitayo; Rowe, Steven M

Book ID: 122233866
Publisher: Elsevier
Year: 2014
Tongue: English
Weight: 336 KB
Volume: 2
Category: Article
ISSN: 2213-2600
DOI: 10.1016/S2213-2600(14)70100-6

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