𝔖 Bobbio Scriptorium
✦   LIBER   ✦

Applied gene therapy in preclinical models of vascular injury

✍ Scribed by Stefan P. Janssens

Book ID
107533725
Publisher
Current Science Inc.
Year
2003
Tongue
English
Weight
331 KB
Volume
5
Category
Article
ISSN
1523-3804

No coin nor oath required. For personal study only.

πŸ“œ SIMILAR VOLUMES

Modeling of congenital erythropoietic po
Modeling of congenital erythropoietic porphyria by RNA interference: a new tool for preclinical gene therapy evaluation
✍ Elodie Robert-Richard; Magalie Lalanne; Isabelle Lamrissi-Garcia; VΓ©ronique Guyo πŸ“‚ Article πŸ“… 2010 πŸ› John Wiley and Sons 🌐 English βš– 357 KB

## Abstract ## Background Congenital erythropoietic porphyria (CEP) is a severe autosomal recessive disorder characterized by a deficiency in uroporphyrinogen III synthase (UROS), the fourth enzyme of the heme biosynthetic pathway. We recently demonstrated the definitive cure of a murine model of