An antisense oligonucleotide against SOD1 delivered intrathecally for patients with SOD1 familial amyotrophic lateral sclerosis: a phase 1, randomised, first-in-man study

✍ Scribed by Miller, Timothy M; Pestronk, Alan; David, William; Rothstein, Jeffrey; Simpson, Ericka; Appel, Stanley H; Andres, Patricia L; Mahoney, Katy; Allred, Peggy; Alexander, Katie; Ostrow, Lyle W; Schoenfeld, David; Macklin, Eric A; Norris, Daniel A; Manousakis, Georgios; Crisp, Matthew; Smith, Richard; Bennett, C Frank; Bishop, Kathie M; Cudkowicz, Merit E

• Book ID: 121445665
• Publisher: The Lancet
• Year: 2013
• Tongue: English
• Weight: 312 KB
• Volume: 12
• Category: Article
• ISSN: 1474-4465
• DOI: 10.1016/S1474-4422(13)70061-9