Acute intermittent porphyria: vector opt
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Makiko Yasuda; Maciej E. Domaradzki; Donna Armentano; Seng H. Cheng; David F. Bi
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Article
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2007
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John Wiley and Sons
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English
⚖ 213 KB
## Abstract ## Background Acute intermittent porphyria (AIP) is an autosomal dominant disorder caused by the half‐normal activity of hydroxymethylbilane synthase (HMB‐synthase). Affected individuals can experience episodic, life‐threatening, acute neurological attacks that are precipitated by vari