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Abstract: 554 AN OPEN-LABEL, DOSE ESCALATION STUDY TO ASSESS THE SAFETY AND EFFICACY OF AAV1-LPLS447X GENE THERAPY WITH ALIPOGENE TIPARVOVEC (AMT-011) FOR PATIENTS WITH SEVERE HYPERTRIGLYCERIDEMIA DUE TO LIPOPROTEIN LIPASE DEFICIENCY (LPLD)

✍ Scribed by Gaudet, D; Brisson, D; Methot, J; van Deventer, S


Book ID
118637126
Publisher
Elsevier Science
Year
2009
Tongue
English
Weight
76 KB
Volume
10
Category
Article
ISSN
1567-5688

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