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A randomized, multicenter, multinational, phase 3B, open-label, parallel-group study of agalsidase beta in treatment-naive male pediatric patients with Fabry disease without severe symptoms: Baseline demographics and clinical data

✍ Scribed by Wijburg, Frits; Bénichou, Bernard; Bichet, Daniel G.; Dostalova, Gabriela; Clarke, Lorne; Fainboim, Alejandro; Fellgiebel, Andreas; Forcelini, Cassiano; Haack, Kristina An; Hopkin, Robert; Scott, C. Ronald; Shankar, Suma; Tylki-Szymanska, Anna; Tøndel, Camilla; Ramaswami, Uma


Book ID
121949235
Publisher
Elsevier Science
Year
2013
Tongue
English
Weight
67 KB
Volume
108
Category
Article
ISSN
1096-7192

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