A phase 1 trial of recombinant human acid Sphingomyelinase (rhASM) Enzyme replacement therapy in adults with Non-Neuronopathic ASM deficiency (ASMD Niemann-Pick B)

✍ Scribed by Margaret McGovern; Melissa Wasserstein; Brian Kirmse; Lane Duvall; Thomas Schiano; Beth Thurberg; Susan Richards; Gerald Cox

• Book ID: 116989192
• Publisher: Elsevier Science
• Year: 2011
• Tongue: English
• Weight: 66 KB
• Volume: 102
• Category: Article
• ISSN: 1096-7192
• DOI: 10.1016/j.ymgme.2010.11.095