A phase 1 enzyme replacement study offers promise for severe hypophospahatasia

A Phase 1/2 Clinical Trial of Enzyme Rep

A Phase 1/2 Clinical Trial of Enzyme Replacement in Fabry Disease: Pharmacokinetic, Substrate Clearance, and Safety Studies

✍ Christine M. Eng; Maryam Banikazemi; Ronald E. Gordon; Martin Goldman; Robert Ph 📂 Article 📅 2001 🏛 American Society of Human Genetics 🌐 English ⚖ 1000 KB

A Randomized Phase 1 Study of Testostero

A Randomized Phase 1 Study of Testosterone Replacement for Patients with Low-Risk Castration-Resistant Prostate Cancer

✍ Russell Szmulewitz; Supriya Mohile; Edwin Posadas; Rangesh Kunnavakkam; Theodore 📂 Article 📅 2009 🏛 Elsevier Science 🌐 English ⚖ 470 KB

Efficacy and safety of enzyme replacemen

Efficacy and safety of enzyme replacement therapy with BMN 110 (elosulfase alfa) for Morquio A syndrome (mucopolysaccharidosis IVA): a phase 3 randomised placebo-controlled study

✍ Hendriksz, Christian J.; Burton, Barbara; Fleming, Thomas R.; Harmatz, Paul; Hug 📂 Article 📅 2014 🏛 Springer 🌐 English ⚖ 358 KB

157. Enzyme replacement therapy with vel

157. Enzyme replacement therapy with velaglucerase alfa significantly improves key clinical parameters in type 1 Gaucher disease: Positive results from a randomized, double-blind, global, phase III study

✍ Ari Zimran; Derlis Gonzalez; Elena A. Lukina; Marie-Françoise Ben Dridi; Isaac K 📂 Article 📅 2010 🏛 Elsevier Science 🌐 English ⚖ 33 KB

Enzyme replacement therapy for mucopolys

Enzyme replacement therapy for mucopolysaccharidosis VI: A phase 3, randomized, double-blind, placebo-controlled, multinational study of recombinant human N-acetylgalactosamine 4-sulfatase (recombinant human arylsulfatase B or rhASB) and follow-on, open-label extension study

✍ Paul Harmatz; Roberto Giugliani; Ida Schwartz; Nathalie Guffon; Elisa Leão Teles 📂 Article 📅 2006 🏛 Elsevier Science 🌐 English ⚖ 276 KB

Enzyme replacement therapy for mucopolys

Enzyme replacement therapy for mucopolysaccharidosis VI: A phase 3, randomized, double-blind, placebo-controlled, multinational study of recombinant human N-acetylgalactosamine 4-sulfatase (recombinant human arylsulfatase B or rhASB) and follow-on, open-label extension study

✍ Paul Harmatz; Roberto Giugliani; Ida Schwartz; Nathalie Guffon; Elisa Leão Teles 📂 Article 📅 2006 🏛 Elsevier Science 🌐 English ⚖ 276 KB