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A novel tool for mapping disease severity and outcomes in patients with Gaucher disease utilising the therapeutic goals

✍ Scribed by Neal Weinreb; Nadia Belmatoug; Bruno Bembi; Olaf Bodamer; Maria Domenica Cappellini; Patrick B. Deegan; Deborah Elstein; Gil Faran; Pilar Gilrado; Derralynn A. Hughes; Eugen Mengel; Gregory M. Pastores; Ari Zimran

Book ID: 116989248
Publisher: Elsevier Science
Year: 2011
Tongue: English
Weight: 63 KB
Volume: 102
Category: Article
ISSN: 1096-7192
DOI: 10.1016/j.ymgme.2010.11.154

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