✦ LIBER ✦

70 Enhanced response to enzyme replacement therapy in Pompe disease following the induction of immune tolerance

✍ Scribed by Dwight D. Koeberl; Baodong Sun; Andrew Bird; Sarah P. Young; Y.-T. Chen; Priya S. Kishnani

Book ID: 116988121
Publisher: Elsevier Science
Year: 2007
Tongue: English
Weight: 41 KB
Volume: 92
Category: Article
ISSN: 1096-7192
DOI: 10.1016/j.ymgme.2007.08.075

No coin nor oath required. For personal study only.

📜 SIMILAR VOLUMES

Immune tolerance induction to enzyme-rep

Immune tolerance induction to enzyme-replacement therapy by co-administration of short-term, low-dose methotrexate in a murine Pompe disease model

✍ A. Joseph; K. Munroe; M. Housman; R. Garman; S. Richards 📂 Article 📅 2008 🏛 John Wiley and Sons 🌐 English ⚖ 303 KB

Partial phenotypic correction and immune

Partial phenotypic correction and immune tolerance induction to enzyme replacement therapy after hematopoietic stem cell gene transfer of α-glucosidase in Pompe disease

✍ Gaëlle Douillard-Guilloux; Emmanuel Richard; Lionel Batista; Catherine Caillaud 📂 Article 📅 2009 🏛 John Wiley and Sons 🌐 English ⚖ 472 KB 👁 1 views

## Abstract ## Background Glycogen storage disease type II (GSDII) or Pompe disease is an inherited disease of glycogen metabolism caused by a lack of functional lysosomal acid α‐glucosidase (GAA). Affected individuals store glycogen in lysosomes resulting in fatal hypertrophic cardiomyopathy and

G.P.8.07 Rate of disease progression and

G.P.8.07 Rate of disease progression and response to enzyme replacement therapy in children and adults with Pompe disease

✍ N.A.M. Van der Beek; J.M. De Vries; C.I. Van Capelle; A.J.J. Reuser; P.A. van Do 📂 Article 📅 2009 🏛 Elsevier Science 🌐 English ⚖ 41 KB

Use of the muscle volume analyzer to eva

Use of the muscle volume analyzer to evaluate enzyme replacement therapy in late-onset Pompe disease

✍ Fuminobu Sugai; Yosuke Kokunai; Yoichi Yamamoto; Goichi Hashida; Kengo Shimazu; 📂 Article 📅 2009 🏛 Springer 🌐 English ⚖ 260 KB

G.P.11.03 Variable response to enzyme re

G.P.11.03 Variable response to enzyme replacement therapy in children and adults with Pompe disease: Need for identification of prognostic factors

✍ N.A.M. van der Beek; C.I. van Capelle; J.M. de Vries; A.J.J. Reuser; P.A. van Do 📂 Article 📅 2008 🏛 Elsevier Science 🌐 English ⚖ 50 KB

Hyaluronidase increases the biodistribut

Hyaluronidase increases the biodistribution of acid α-1,4 glucosidase in the muscle of Pompe disease mice: An approach to enhance the efficacy of enzyme replacement therapy

✍ Reuben Matalon; Sankar Surendran; Gerald A. Campbell; Kimberlee Michals-Matalon; 📂 Article 📅 2006 🏛 Elsevier Science 🌐 English ⚖ 363 KB