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55. An adjunct rhGAA ERT-small molecule treatment approach for Pompe disease: Pharmacological chaperone AT2220 prevents rhGAA denaturation and loss of enzyme activity

✍ Scribed by John J. Flanagan; Richie Khanna; George Neusch; Jessie Feng; Michelle Zdancewicz; Brian Ranes; Rebecca Soska; Terry Yin; Ken J. Valenzano; David J. Lockhart; Hung V. Do


Book ID
116988489
Publisher
Elsevier Science
Year
2009
Tongue
English
Weight
43 KB
Volume
96
Category
Article
ISSN
1096-7192

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