𝔖 Bobbio Scriptorium
✦   LIBER   ✦

35 Preclinical model for gene therapy: Role of the host

✍ Scribed by M.P. Colombo; G. Fomi; A. Stoppacciaro


Book ID
116166791
Publisher
Elsevier Science
Year
1995
Tongue
English
Weight
159 KB
Volume
31
Category
Article
ISSN
0959-8049

No coin nor oath required. For personal study only.


πŸ“œ SIMILAR VOLUMES


Modeling of congenital erythropoietic po
✍ Elodie Robert-Richard; Magalie Lalanne; Isabelle Lamrissi-Garcia; VΓ©ronique Guyo πŸ“‚ Article πŸ“… 2010 πŸ› John Wiley and Sons 🌐 English βš– 357 KB

## Abstract ## Background Congenital erythropoietic porphyria (CEP) is a severe autosomal recessive disorder characterized by a deficiency in uroporphyrinogen III synthase (UROS), the fourth enzyme of the heme biosynthetic pathway. We recently demonstrated the definitive cure of a murine model of